About Orphina
Founded by pioneers in understanding and catalyzing progress in GNE Myopathy (GNEM), …
Orphina's Name
Orphina is derived from “Orphan”, defined as “one deprived of protection or advantage”. We are the reason justifying the need for the Orphan Drug Act, and the need for rapid innovation towards development of cures.
Our Misson
Using both novel and ignored technologies to maximize therapeutic benefit to human quality of life.
Our Vision
Build a top-tier independent biotechnology company that gathers the resources needed to accelerate the clinical development of very effective treatments.
Our Core Values
Commitment to Patients, Innovation and Discovery, Sense of Urgency, Open Culture, Passion for Excellence.